PI Agency Title Jeffrey Bednarski HRSA/University of California, San Francisco Severe Combined Immunodeficiency (SCID) Screening and Education Thomas Ferkol State of Missouri Genetics Program, Newborn Cystic Fibrosis-Region 3 Jessica Pittman CFF/Seattle Children’s Hospital A Prospective Study to Evaluate Biological and Clinical Effects of Significantly Corrected CFTR Function (The PROMISE Study) …