Funded Awards April 2020
PI Agency Title Leonard Bacharier NIH/ U2C/Duke University ECHO Coordinating Center Jeffrey Bednarski NIH/U54/Regents of University of California – San Francisco Primary Immune Deficiency Treatment Consortium Brian DeBosch AASLD Hepatic Arginase 2 as a Novel Fasting-induced Factor to Treat NAFLD and NASH Lori Holtz NIH/R01 Role of Environmental Exposures …
Funded Awards March 2020
PI Agency Title Jagruti Anadkat NIH/R01/University of Michigan Sleep-disordered Breathing in Infants with Myelomeningocele Aimee Baumann-Dudenhoeffer NIH/R03 Longitudinal Effects of Diet and the Gut Microbiome on Immunosuppressive Drug Metabolism Juliane Bubeck Wardenburg Washington University Center for Drug Discovery/ Matching Micro Grant LEAP: Single optimized novel formulation of alpha-toxin vaccine …
Funded Awards January 2020
PI Agency Title Jonathan Cooper ForeBatten Foundation Defining Peripheral and Enteric Nervous System disease in Juvenile Batten Disease Jonathan Cooper Abeona Neuropathologic Evaluation of the Efficacy of Intrathecal AAV9-Mediated Gene Therapy for Cln1 Disease Jorge Di Paola NIH/R01 Genomics of Megakaryocyte and Platelet Biology Andrea Granados CDTR Safety and …
December 2019 Funded Awards
PI Agency Title Regina Clemens CIMED Developmental regulation of neutrophil calcium signaling by KCa3.1 Jonathan Cooper Giving Back Foundation Developing Enzyme Replacement Therapy in a Sheep Model of CLN1 disease or Infantile Neuronal Ceroid Lipofuscinosis Jorge Di Paola SLCH Foundation/Research Grant Neuro Oncology and Investigational New Drug Support Year …
November 2019 Funded Awards
PI Agency Title Patricia Dickson NIH/ R61/R33 Recombinant Alpha-N-Acetylglucosaminidase with Improved Mannose 6-Phosphorylation for Treatment of Sanfilippo B Syndrome Jane Garbutt SLCH Foundation WU PAARC Mental Health Care Collaborative Misty Good Takeda Takeda Sponsored Research Agreement Peter Michelson CFF/University of North Carolina at Chapel Hill Assessing Effectiveness of CF …
October Funded Grants
PI Agency Title Sesh Cole CHOP CHOP / PEDSnet Data Coordinating Center 2 Megan Cooper SLCH Foundation Modell Foundation- Family Assistance Award Patricia Dickson NIH/SBIR/STTR/Tega Therapeutics Intracerebroventricular Alpha-N-Acetylglucosaminidase Delivery to the Brain Patricia Dickson Genzyme The Role of Angiotensin II-Mediated Inflammation in MPS I Vascular Disease: A study of …
September 2019 Funded Awards
PI Agency Title Fahd Ahmad NIH/R18 Implementation of Electronic Health Screening in Primary Care to Improve STI Testing Leonard Bacharier American Lung Association/University of Kansas Medical Center Asthma Clinical Research Center (ACRC) Leonard Bacharier NIH/UG1/University of Kansas Medical Center Precision Biologic Interventions for Severe Exacerbation Prone Asthma (PRECISE) Clinical Center …
August Funded Awards
PI Agency Title Patricia Dickson SLCH Foundation Down Syndrome Speaker Peter Michelson CFF/Boston Children’s Hospital Feasibility, Acceptability, and Randomized Controlled Trial of a Tele-coaching Intervention to Improve Treatment Adherence in Cystic Fibrosis (Telecoaching) Michael Thompson NIH/K08 Impact of Maternal Obesity on Offspring Non-alcoholic Fatty Liver Disease: Role of Bile …
Funded Awards July
PI Agency Title Sesh Cole CHOP CHOP/Invokana Sesh Cole SLCH Foundation/Restricted Funding Request Feather Donation Brian DeBosch NIH/R21 Biological Effects and Mechanistic Actions of the Natural Disaccharide and Dietary Supplement, Trehalose. Amjad Horani NIH/K08 The Role of Dynein Motor Mutations in Motile Cilia Disease Kim Liss Washington …
Funded Awards June
PI Agency Title Aimee Baumann-Dudenhoeffer Wash U CRTC/Doris Duke (DDFRCS) Impact of the Gut Microbiome on Individualized Tacrolimus Pharmacokinetics Jeffrey Bednarski NIH/U01/University of California, San Francisco PBMTC Study NMD 1801 – CSIDE Nicole Brossier SLCH Foundation Defining the molecular mechanisms underlying pediatric brain tumor penetrance Nicole Brossier Alex’s …